Replacing mannose-6-phosphate with engineered IGF2 for precision delivery.
In mouse models, our IGF2-mediated approach has demonstrated a massive leap in enzyme delivery efficiency compared to standard ERTs:
| Tissue Target | Efficiency vs. Standard ERT |
|---|---|
| Heart | 10x Higher |
| Skeletal Muscle | 7x Higher |
| Lung | 6x Higher |
| Kidney | 5x Higher |